Morquio syndrome is a very rare inherited disease. It is called mucopolysaccharidosis because the body cannot break down mucopolysaccharides which make up mucous. It has very serious effects, but can be helped by a synthetic version of the enzyme which is not working.
References[change | change source]
- "MPS IV (Morquio syndrome)". MPSSociety.org. National MPS Society. Archived from the original on 21 August 2017. Retrieved 14 January 2015.
- "FDA approves Vimizim to treat rare congenital enzyme disorder" (Press release). US Food and Drug Administration. 14 February 2014. Retrieved 14 January 2015.