Morquio syndrome

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Morquio syndrome is a very rare inherited disease. It is called mucopolysaccharidosis because the body cannot break down mucopolysaccharides which make up mucous.[1] It has very serious effects, but can be helped by a synthetic version of the enzyme which is not working.[2]

References[change | change source]

  1. "MPS IV (Morquio syndrome)". National MPS Society. Retrieved 14 January 2015.
  2. US Food and Drug Administration (14 February 2014). "FDA approves Vimizim to treat rare congenital enzyme disorder". Press release. Retrieved 14 January 2015.